Biology 9700 · AS & A Level · Genetic technology applied to medicine

Genetic technology applied to medicine — practice question

If blood supply to the brain is cut down severely, brain cells die; this event is known as a stroke. The outcomes after a stroke can vary from recovery to lasting brain damage and death. A newly developed emergency gene therapy for people who may develop brain damage after a stroke was tested in mice. • The human granulocyte colony-stimulating factor, hG-CSF, is a protein that encourages stem cell production in bone marrow. • mRNA coding for hG-CSF was isolated and then used to produce cDNA. • This cDNA was inserted into an adeno-associated virus (AAV) vector and delivered in eye drops to mice immediately after they had a stroke.
(a(i))[2]

Explain the meaning of gene therapy.

(a(ii))[2]

Describe the roles of reverse transcriptase and DNA polymerase when making cDNA for hG-CSF.

(a(iii))[2]

The AAV vector used was unable to copy itself inside the target cells. Suggest why the researchers selected a vector that could not replicate.

(b(i))[3]

Explain why the mice in group D were included in the study.

(b(ii))[1]

Explain why the mice in group D were included in the study.

(c)[4]

Use the results in Table 5.1 to evaluate the benefits of gene therapy treatment, with AAV vector carrying the gene for hG-CSF, for people who have a stroke.

Worked solution & mark scheme

This 14-mark question has a full step-by-step worked solution and mark scheme. One marking point: A disease arising from a faulty recessive allele

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